(Reuters Health) – Scientists have identified four specific, dominant variants of the SPTLC1 gene in 11 children from seven different
Continue reading »Home »
Spinal Muscular Atrophy Drug Approved in Europe
The European Commission (EC) has granted marketing clearance for risdiplam (Evrysdi, PTC Therapeutics), the first oral treatment for patients with
Continue reading »Novartis: About two million dollars per single dose – the most expensive drug approved in the world
World’s most expensive drug: a drug against muscle disease admitted to the The Swiss pharmaceutical company Novartis has received US
Continue reading »