(Reuters Health) – Scientists have identified four specific, dominant variants of the SPTLC1 gene in 11 children from seven different
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Spinal Muscular Atrophy Drug Approved in Europe
The European Commission (EC) has granted marketing clearance for risdiplam (Evrysdi, PTC Therapeutics), the first oral treatment for patients with
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Novartis: About two million dollars per single dose – the most expensive drug approved in the world
World’s most expensive drug: a drug against muscle disease admitted to the The Swiss pharmaceutical company Novartis has received US
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